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Nucleotide Precursor
Nucleotide Precursors for TK2 Deficiency
Recruiting1 awardPhase 1 & 2
New York City, New York
This trial is for patients with a mitochondrial DNA depletion syndrome caused by a thymidine kinase 2 deficiency. The treatment is open label deoxythymidine and deoxycytidine, which are nucleotide precursors that may help reduce clinical symptoms by increasing the number of functional mitochondrial DNA.
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