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Enzyme Replacement Therapy
Elaprase +1 More for Mucopolysaccharidosis
Recruiting1 award2 criteria
Philadelphia, Pennsylvania
As the HGT-HIT-046 (NCT01506141) and SHP609-302 (NCT02412787) studies will be closed, this post-trial access (PTA) program provides TAK-609 to participants in these studies for whom the benefit:risk ratio of continued treatment with idursulfase-IT remains positive.
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