Dr. Perry Shieh, MD, PhD
Claim this profileDavid Geffen School of Medicine at UCLA
Affiliated Hospitals
David Geffen School Of Medicine At UCLA
UCLA
Clinical Trials Perry Shieh, MD, PhD is currently running
Zolgensma
for Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a neurogenetic disorder caused by a loss or mutation in the survival motor neuron 1 gene (SMN1) on chromosome 5q13, which leads to reduced SMN protein levels and a selective dysfunction of motor neurons. SMA is an autosomal recessive, early childhood disease with an incidence of 1:10,000 live births. SMA is the leading cause of infant mortality due to genetic diseases. The purpose of this registry is to assess the long term outcomes of patients with SMA in the context of advances in treatment options and also to characterize and assess long-term safety and effectiveness of OAV-101.
Recruiting
1 award
N/A
2 criteria
Endpoint Assessment
for Myotonic Dystrophy
The overall goal of the study is to establish valid clinical endpoint assessments for children with congenital myotonic dystrophy type 1 and develop biomarkers for the condition.
Recruiting
1 award
N/A
3 criteria
More about Perry Shieh, MD, PhD
Clinical Trial Related
2 years of experience running clinical trials · Led 15 trials as a Principal Investigator · 6 Active Clinical Trials
Treatments Perry Shieh, MD, PhD has experience with
- Placebo
- Tideglusib
- Motor Outcomes To Validate Evaluations In FSHD (MOVE FSHD)
- Delandistrogene Moxeparvovec
- ABC008
- ManNAc
Breakdown of trials Perry Shieh, MD, PhD has run
Duchenne Muscular Dystrophy
Myotonic Dystrophy
Inclusion Body Myositis
Facioscapulohumeral Muscular Dystrophy
Other Doctors you might be interested in
Frequently asked questions
Do I need insurance to participate in a trial?
Almost all clinical trials will cover the cost of the ‘trial drug’ — so no insurance is required for this. For trials where this trial drug is given alongside an already-approved medication, there may be a cost (which your insurance would normally cover).
What does Perry Shieh, MD, PhD specialize in?
Perry Shieh, MD, PhD focuses on Duchenne Muscular Dystrophy and Myotonic Dystrophy. In particular, much of their work with Duchenne Muscular Dystrophy has involved dystrophin positive patients, or patients who are undergoing treatment.
Is Perry Shieh, MD, PhD currently recruiting for clinical trials?
Yes, Perry Shieh, MD, PhD is currently recruiting for 6 clinical trials in Los Angeles California. If you're interested in participating, you should apply.
Are there any treatments that Perry Shieh, MD, PhD has studied deeply?
Yes, Perry Shieh, MD, PhD has studied treatments such as Placebo, Tideglusib, Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD).
What is the best way to schedule an appointment with Perry Shieh, MD, PhD?
Apply for one of the trials that Perry Shieh, MD, PhD is conducting.
What is the office address of Perry Shieh, MD, PhD?
The office of Perry Shieh, MD, PhD is located at: David Geffen School of Medicine at UCLA, Los Angeles, California 90095 United States. This is the address for their practice at the David Geffen School of Medicine at UCLA.
Is there any support for travel costs?
The coverage of travel expenses can vary greatly between different clinical trials. Please see more financial detail in the trials you’re interested to apply.
Unbiased Results
We believe in providing patients with all the options.
Your Data Stays Your Data
We only share your information with the clinical trials you're trying to access.
Verified Trials Only
All of our trials are run by licensed doctors, researchers, and healthcare companies.