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Virus Therapy

FLT201 for Gaucher Disease

Phase 1 & 2
Recruiting
Research Sponsored by Freeline Therapeutics
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
Be older than 18 years old
Must not have
n/a
Timeline
Screening 3 weeks
Treatment Varies
Follow Up week 38 to month 60
Awards & highlights
No Placebo-Only Group

Summary

This trial will follow participants with Gaucher disease type 1 who were previously treated with FLT201 in a different trial. The participants will be monitored for 5 years after the treatment.

Who is the study for?
This trial is for individuals with Type-1 Gaucher Disease who have previously received FLT201 treatment in an earlier study. They will be monitored over a period of 5 years to understand the long-term effects of the treatment.
What is being tested?
The trial is observing the long-term outcomes and safety of FLT201, a therapy for Type-1 Gaucher Disease, by following participants from a previous clinical study over five years after their last dose.
What are the potential side effects?
Since this is a follow-up study, specific side effects are not listed; however, it will monitor any long-term health changes that may relate to prior FLT201 treatment.

Eligibility Criteria

Exclusion Criteria

You may be eligible for the trial if you check “No” for criteria below:
Select...
N/A

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~week 38 to month 60
This trial's timeline: 3 weeks for screening, Varies for treatment, and week 38 to month 60 for reporting.

Treatment Details

Study Objectives

Study objectives can provide a clearer picture of what you can expect from a treatment.
Primary study objectives
Incidence of treatment-emergent adverse events (TEAEs) (including DLTs)

Awards & Highlights

No Placebo-Only Group
All patients enrolled in this study will receive some form of active treatment.

Trial Design

1Treatment groups
Experimental Treatment
Group I: Dosed with FLT201Experimental Treatment1 Intervention

Find a Location

Who is running the clinical trial?

Freeline TherapeuticsLead Sponsor
6 Previous Clinical Trials
77 Total Patients Enrolled
1 Trials studying Gaucher Disease
18 Patients Enrolled for Gaucher Disease
Spur TherapeuticsLead Sponsor
6 Previous Clinical Trials
77 Total Patients Enrolled
1 Trials studying Gaucher Disease
18 Patients Enrolled for Gaucher Disease
~50 spots leftby May 2029
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