40 Participants Needed

Microbiome Evaluation for Graft-versus-Host Disease

BK
Overseen ByBetty K Hamilton, MD
Age: 18+
Sex: Female
Trial Phase: Academic
Sponsor: Case Comprehensive Cancer Center
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

This trial examines how the vaginal microbiome (the community of bacteria, fungi, and viruses in the body) changes in women undergoing allogeneic HCT, a type of stem cell transplant. The researchers aim to determine if these changes are linked to vulvovaginal graft-versus-host disease, a condition affecting the vagina and vulva. Women planning to undergo this transplant or who have already had it and developed symptoms are suitable candidates for this study. Participants will undergo vaginal exams and symptom assessments before the transplant and at regular intervals afterward. As a Phase 2 trial, this research focuses on measuring the treatment's effectiveness in an initial, smaller group, allowing participants to contribute to significant findings.

Do I need to stop my current medications for this trial?

The trial information does not specify whether you need to stop taking your current medications. It is best to discuss this with the trial coordinators or your doctor.

What prior data suggests that this observational study is safe?

Research has shown that allogeneic hematopoietic cell transplantation (HCT) has been thoroughly studied for safety. Studies have found that severe liver issues and the most serious forms of liver-related graft-versus-host disease (GVHD) are now much less common. Improved transplant techniques and care have led to this progress. However, some side effects can still occur. About 44% of patients might experience GVHD, but only around 15% of these cases are severe. While risks exist, medical care can manage many side effects. Overall, the treatment is generally well-tolerated, but participants must stay informed and be closely monitored during and after the procedure.12345

Why are researchers excited about this trial?

Researchers are excited about this trial because it aims to improve the diagnosis and understanding of vulvovaginal graft-versus-host disease (GVHD) by evaluating the microbiome of patients undergoing allogeneic hematopoietic cell transplantation (HCT). Unlike standard treatments for GVHD, which focus on managing symptoms with immunosuppressive drugs, this research explores the potential role of the vaginal microbiome in the disease's development and progression. By gaining insights into the microbial environment, researchers hope to uncover new diagnostic markers or therapeutic targets that could lead to more effective, personalized treatment strategies in the future.

What evidence suggests that this study's methods could help understand vulvovaginal GVHD?

Allogeneic hematopoietic cell transplantation (HCT) uses donor stem cells to treat patients with blood-related diseases. Research has shown that it can provide long-term benefits, with about 40% of patients living for many years post-treatment. This method is particularly beneficial for older patients with blood cancers, offering a potential cure. However, challenges include the risk of disease recurrence and infections after the transplant. This study focuses on vulvovaginal graft-versus-host disease (GVHD) in participants undergoing allogeneic HCT, but understanding HCT's effectiveness aids in improving overall patient outcomes.36789

Who Is on the Research Team?

BK

Betty K Hamilton, MD

Principal Investigator

Cleveland Clinic Taussig Cancer Institute, Case Comprehensive Cancer Center

Are You a Good Fit for This Trial?

Inclusion Criteria

I am a woman planning to have or have had a stem cell transplant and am experiencing vulvovaginal issues.
My treatment includes any type of stem cell source.
I am between 18 and 70 years old.
See 6 more

Timeline for a Trial Participant

Screening

Participants are screened for eligibility to participate in the trial

2-4 weeks

Pre-transplant Assessment

Participants undergo a vulvovaginal symptom questionnaire and vaginal microbiome evaluation

1 visit
1 visit (in-person)

Post-transplant Follow-up

Participants are monitored for changes in the vaginal microbiome and symptoms of vulvovaginal GVHD at 6 and 12 months post-transplant

12 months
2 visits (in-person) at 6 and 12 months

Symptom-triggered Assessment

Additional vaginal exams are conducted if symptoms of vulvovaginal GVHD develop

What Are the Treatments Tested in This Trial?

Interventions

  • Vaginal Microbiome Evaluation

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Allogeneic HCT participantsExperimental Treatment2 Interventions

Find a Clinic Near You

Who Is Running the Clinical Trial?

Case Comprehensive Cancer Center

Lead Sponsor

Trials
472
Recruited
33,400+

Incyte Corporation

Industry Sponsor

Trials
408
Recruited
66,800+
Steven Stein profile image

Steven Stein

Incyte Corporation

Chief Medical Officer since 2015

MD from University of Witwatersrand

Hervé Hoppenot profile image

Hervé Hoppenot

Incyte Corporation

Chief Executive Officer since 2014

MBA from ESSEC Business School

Citations

Long-Term Results of Hematopoietic Cell Transplantation ...

Allo-HCT produced 5-year and 10-year OS rates of 37.8% and 30.6%, respectively, while 5-year and 10-year PFS rates were 31.4% and 24.7%, ...

The 2023 EBMT report on hematopoietic cell ...

When compared to the 2022 data, an overall increase of +3.4% was observed (+7.8% allogeneic HCT and +0.4% autologous HCT). In addition, there ...

Treatment Trends and Outcomes of Allogeneic ...

50% of transplanted ALL patients are alive with good long-term survival of 40%. Lack of availability of prohibitively expensive novel agents ...

Outcomes of Allogeneic Hematopoietic Stem Cell ...

Allo-HCT offers curative potential for patients aged 70 and above with hematologic malignancies. •. Post-transplant relapse and infection remain the leading ...

Review Allogeneic Hematopoietic Cell Donor Selection

Outcomes of HCT using matched unrelated donors (8/8 allele HLA-matched, MUDs) now result in similar outcomes to recipients of MSD HCT, in part ...

Improved outcomes with allogeneic hematopoietic cell ...

Severe liver dysfunction is now much less common following allogeneic HCT, and grade IV hepatic GVHD has all but disappeared. Based on observations that ...

Improving Safety and Outcomes After Allogeneic ...

This study reports the results of outcomes-directed improvements in transplantation design, GVHD prophylaxis, and supportive care

Better clinical outcomes and lower triggering of ...

Home-based treatment following Allo-HCT yields multiple promising clinical outcomes and improved systemic inflammatory markers, which may contribute to less ...

Outcomes of allogeneic hematopoietic cell transplantation ...

Adverse events related to all-HCT were manageable with rates of acute and chronic graft-versus-host disease in 44.0% (39.6-48.4%; grade III/IV: 15.2%) and 46.5% ...