Achondroplasia Clinical Trials 2023

Achondroplasia research studies recruiting patients in 2023 need your help. Receive premium care & cutting edge treatments by enrolling in achondroplasia clinical trials today.

Popular Trials

Peptide

BMN 111 for Achondroplasia

Recruiting1 awardPhase 2

Oakland, California

This trial is to study the long-term effects of a medication given to children with achondroplasia, a form of dwarfism. The study will track the children's safety and tolerability of the medication over a period of time.

Popular Filters

Trials for ACH Patients

TYRA-300 for Achondroplasia

Recruiting1 awardPhase 2

Kissimmee, Florida

This trial aims to assess how safe and well-tolerated TYRA-300 is in children with achondroplasia who still have open growth plates, and to determine the most effective dose(s

Kinase Inhibitor

Infigratinib for Achondroplasia

Recruiting1 awardPhase 3

San Francisco, California

This trial tests a drug to help children and teens with achondroplasia. It's randomized, double-blind, and placebo-controlled.

Growth Hormone Therapy

Navepegritide for Achondroplasia

Recruiting0 awardsPhase 2

Houston, Texas

"This trial will test the safety and effectiveness of a new medication called Navepegritide in infants under 2 years old with a specific genetic condition. The medication will be given once a week

Procedure

TransCon CNP for Achondroplasia

Recruiting1 awardPhase 2 & 3

Little Rock, Arkansas

This trial uses TransCon CNP to help children and adolescents with achondroplasia grow their bones properly. It is for those who have already been part of a previous trial. The treatment continues for an extended period.

Peptide

TransCon CNP for Achondroplasia

Recruiting0 awardsPhase 2 & 3

Saint Paul, Minnesota

This trial tests if regular injections can help children with Achondroplasia grow taller by making their bones grow faster. Vosoritide has shown promising results in increasing growth in children with achondroplasia.

Tyrosine Kinase Inhibitor

Infigratinib for Achondroplasia

Recruiting1 awardPhase 2

Wilmington, Delaware

This trial studies the long-term safety, tolerability, and efficacy of a drug to treat ACH, and also assesses the quality of life of those affected.

Trials With No Placebo

TYRA-300 for Achondroplasia

Recruiting1 awardPhase 2

Kissimmee, Florida

This trial aims to assess how safe and well-tolerated TYRA-300 is in children with achondroplasia who still have open growth plates, and to determine the most effective dose(s

Procedure

TransCon CNP for Achondroplasia

Recruiting1 awardPhase 2 & 3

Little Rock, Arkansas

This trial uses TransCon CNP to help children and adolescents with achondroplasia grow their bones properly. It is for those who have already been part of a previous trial. The treatment continues for an extended period.

Tyrosine Kinase Inhibitor

Infigratinib for Achondroplasia

Recruiting1 awardPhase 2

Wilmington, Delaware

This trial studies the long-term safety, tolerability, and efficacy of a drug to treat ACH, and also assesses the quality of life of those affected.

Tyrosine Kinase Inhibitor

Infigratinib for Achondroplasia

Recruiting1 awardPhase 2

Wilmington, Delaware

This trial is testing a medicine called infigratinib in children aged 3 to 11 years with Achondroplasia. The medicine works by blocking proteins that cause abnormal bone growth. The children have already participated in an earlier study.

Peptide

BMN 111 for Achondroplasia

Recruiting2 awardsPhase 2

Oakland, California

This trial is testing BMN111, an injection, in children with Achondroplasia to help them grow taller. BMN111 has shown promise in promoting growth in children with achondroplasia.

Peptide

BMN 111 for Achondroplasia

Recruiting2 awardsPhase 3

Oakland, California

This trial is testing if a new drug, BMN 111, is a safe and effective treatment for children with achondroplasia.

Frequently Asked Questions

Do I need insurance to participate in a trial?

Almost all clinical trials will cover the cost of the 'trial drug' — so no insurance is required for this. For trials where this trial drug is given alongside an already-approved medication, there may be a cost (which your insurance would normally cover).

Is there any support for travel costs?

Many of the teams running clinical trials will cover the cost of transportation to-and-from their care center.

Will I know what medication I am taking?

This depends on the specific study. If you're worried about receiving a placebo, you can actively filter out these trials using our search.

How long do clinical trials last?

Some trials will only require a single visit, while others will continue until your disease returns. It's fairly common for a trial to last somewhere between 1 and 6 months.

Do you verify all the trials on your website?

All of the trials listed on Power have been formally registered with the US Food and Drug Administration. Beyond this, some trials on Power have been formally 'verified' if the team behind the trial has completed an additional level of verification with our team.

How quickly will I hear back from a clinical trial?

Sadly, this response time can take anywhere from 6 hours to 2 weeks. We're working hard to speed up how quickly you hear back — in general, verified trials respond to patients within a few days.