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Trials for AS Patients
Behavioural Intervention
Virtual Therapy for Developmental Disabilities
Recruiting1 award8 criteria
Chicago, Illinois
This trial tests a virtual therapy program to help people with intellectual and developmental disorders better communicate and manage their behavior. Participants will do assessments and have weekly or biweekly virtual visits with a therapist.
GABA Receptor Agonist
Alogabat for Angelman Syndrome
Recruiting1 awardPhase 2
Chicago, Illinois
This trial tests Alogabat, a medication, to see if it can help children aged 5-17 with deletion Angelman Syndrome. Researchers will give the medication daily and check for improvements in brain activity over a few months.
Antisense Oligonucleotide
ION582 for Angelman Syndrome
Recruiting1 awardPhase 1 & 2
Chicago, Illinois
This trial is testing a drug called ION582, given directly into the spinal fluid, to see if it is safe for people with Angelman syndrome. The study will check how well patients tolerate different doses of the drug.
RO7248824 for Angelman Syndrome
Recruiting1 awardPhase 1
Los Angeles, California
This trial is a study to test a new drug for safety, tolerability, and how well it works. The study will enroll two groups of children, those aged 5-12 and those aged 1-4, and will test different doses of the drug in each group.
Trials With No Placebo
Behavioural Intervention
Virtual Therapy for Developmental Disabilities
Recruiting1 award8 criteria
Chicago, Illinois
This trial tests a virtual therapy program to help people with intellectual and developmental disorders better communicate and manage their behavior. Participants will do assessments and have weekly or biweekly virtual visits with a therapist.
GABA Receptor Agonist
Alogabat for Angelman Syndrome
Recruiting1 awardPhase 2
Chicago, Illinois
This trial tests Alogabat, a medication, to see if it can help children aged 5-17 with deletion Angelman Syndrome. Researchers will give the medication daily and check for improvements in brain activity over a few months.
Antisense Oligonucleotide
ION582 for Angelman Syndrome
Recruiting1 awardPhase 1 & 2
Chicago, Illinois
This trial is testing a drug called ION582, given directly into the spinal fluid, to see if it is safe for people with Angelman syndrome. The study will check how well patients tolerate different doses of the drug.
RO7248824 for Angelman Syndrome
Recruiting1 awardPhase 1
Los Angeles, California
This trial is a study to test a new drug for safety, tolerability, and how well it works. The study will enroll two groups of children, those aged 5-12 and those aged 1-4, and will test different doses of the drug in each group.
Behavioural Intervention
PIXI for Neurogenetic Disorders
Recruiting1 award2 criteria
Research Triangle Park, North Carolina
This trial tests a program called PIXI, which helps parents of infants with genetic disorders. The program educates parents about their baby's condition, coaches them on how to interact with their baby, and provides family support. The goal is to improve the baby's development and family well-being.
Frequently Asked Questions
Do I need insurance to participate in a trial?
Almost all clinical trials will cover the cost of the 'trial drug' — so no insurance is required for this. For trials where this trial drug is given alongside an already-approved medication, there may be a cost (which your insurance would normally cover).
Is there any support for travel costs?
Many of the teams running clinical trials will cover the cost of transportation to-and-from their care center.
Will I know what medication I am taking?
This depends on the specific study. If you're worried about receiving a placebo, you can actively filter out these trials using our search.
How long do clinical trials last?
Some trials will only require a single visit, while others will continue until your disease returns. It's fairly common for a trial to last somewhere between 1 and 6 months.
Do you verify all the trials on your website?
All of the trials listed on Power have been formally registered with the US Food and Drug Administration. Beyond this, some trials on Power have been formally 'verified' if the team behind the trial has completed an additional level of verification with our team.
How quickly will I hear back from a clinical trial?
Sadly, this response time can take anywhere from 6 hours to 2 weeks. We're working hard to speed up how quickly you hear back — in general, verified trials respond to patients within a few days.