Metabolic Camp for Pregnant Women with Phenylketonuria
Recruiting1 award4 criteria
Atlanta, Georgia
This trial will study whether teaching teens and young women with Phenylketonuria (PKU) or Maple Syrup Urine Disease (MSUD) about their disease and nutrition in a camp environment improves pregnancy outcomes.
Popular Filters
Trials for PKU Patients
Behavioral Intervention
Coping Skills Intervention for Phenylketonuria
Recruiting1 award1 criteria
Columbia, Missouri
"This trial aims to study the effectiveness of a short-term psychosocial therapy called Show Me FIRST for treating anxiety and depression in adolescents with PKU. The researchers also want to validate new assessment measures that
Procedure
JNT-517 for Phenylketonuria
Recruiting0 awardsPhase 1
Atlanta, Georgia
This trial tests a new oral medication, JNT-517, for safety and tolerance. It involves healthy participants and people with phenylketonuria (PKU). Researchers aim to see if JNT-517 can safely reduce certain amino acids in people with PKU.
Enzyme substitution therapy
Pegvaliase for Phenylketonuria
Recruiting2 awardsPhase 3
Aurora, Colorado
This trial is testing pegvaliase injections in adolescents with PKU. The goal is to see if these injections are safe and effective. Pegvaliase helps the body break down a harmful substance that people with PKU cannot process on their own. Pegvaliase is a newer treatment for PKU, following earlier treatments like dietary restriction and sapropterin.
Trials With No Placebo
Behavioral Intervention
Coping Skills Intervention for Phenylketonuria
Recruiting1 award1 criteria
Columbia, Missouri
"This trial aims to study the effectiveness of a short-term psychosocial therapy called Show Me FIRST for treating anxiety and depression in adolescents with PKU. The researchers also want to validate new assessment measures that
Enzyme substitution therapy
Pegvaliase for Phenylketonuria
Recruiting2 awardsPhase 3
Aurora, Colorado
This trial is testing pegvaliase injections in adolescents with PKU. The goal is to see if these injections are safe and effective. Pegvaliase helps the body break down a harmful substance that people with PKU cannot process on their own. Pegvaliase is a newer treatment for PKU, following earlier treatments like dietary restriction and sapropterin.
PTC923 for Phenylketonuria
Recruiting2 awardsPhase 3
Aurora, Colorado
This trial is testing the safety of a medication called PTC923 in people with phenylketonuria (PKU). PKU patients need to manage their blood phenylalanine levels carefully. PTC923 aims to help control these levels, making it easier for patients to manage their condition. PTC923 is a newer treatment for PKU, following earlier treatments like sapropterin and pegvaliase.
Frequently Asked Questions
Do I need insurance to participate in a trial?
Almost all clinical trials will cover the cost of the 'trial drug' — so no insurance is required for this. For trials where this trial drug is given alongside an already-approved medication, there may be a cost (which your insurance would normally cover).
Is there any support for travel costs?
Many of the teams running clinical trials will cover the cost of transportation to-and-from their care center.
Will I know what medication I am taking?
This depends on the specific study. If you're worried about receiving a placebo, you can actively filter out these trials using our search.
How long do clinical trials last?
Some trials will only require a single visit, while others will continue until your disease returns. It's fairly common for a trial to last somewhere between 1 and 6 months.
Do you verify all the trials on your website?
All of the trials listed on Power have been formally registered with the US Food and Drug Administration. Beyond this, some trials on Power have been formally 'verified' if the team behind the trial has completed an additional level of verification with our team.
How quickly will I hear back from a clinical trial?
Sadly, this response time can take anywhere from 6 hours to 2 weeks. We're working hard to speed up how quickly you hear back — in general, verified trials respond to patients within a few days.