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Potassium Channel Activator

Diazoxide for Non-alcoholic Fatty Liver Disease

Phase 1
Recruiting
Led By Joshua R Cook, MD, PhD
Research Sponsored by Columbia University
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
Be older than 18 years old
Timeline
Screening 3 weeks
Treatment Varies
Follow Up up to study day 15

Summary

This trial will compare 2 doses of diazoxide to placebo to see how they affect glucose and fat metabolism in people with IR-NAFLD. Participants will take 27 doses, have fasting blood tests and wear a glucose monitor for 14 days.

Who is the study for?
Adults aged 18-70 with overweight/obesity and insulin resistance, at high risk for or diagnosed with NAFLD. Must have prediabetes indicators like fasting plasma glucose of 100-125 mg/dL or HbA1c of 5.7-6.4%. Excludes those with diabetes, abnormal heart rates, recent significant weight loss, certain medical conditions including active COVID-19 within screening period, psychiatric diseases decompensated within a year, known allergies to trial drugs, and women not using effective contraception.
What is being tested?
The trial tests diazoxide's effect on glucose and lipid metabolism in people with insulin resistance and NAFLD over two weeks. Participants will take diazoxide (1 or 2 mg per kg) or placebo daily while monitoring blood sugar continuously and having regular blood draws to measure the impact on plasma glucose and serum lipids.
What are the potential side effects?
Potential side effects include low blood sugar levels due to its action as an insulin inhibitor which might cause dizziness or fainting; fluid retention leading to swelling in legs; increased uric acid levels possibly resulting in gout; fatigue; headache; nausea; heart-related issues such as palpitations.

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~up to study day 15
This trial's timeline: 3 weeks for screening, Varies for treatment, and up to study day 15 for reporting.

Treatment Details

Study Objectives

Study objectives can provide a clearer picture of what you can expect from a treatment.
Primary study objectives
Fasting plasma glucose (absolute values)
Fasting plasma glucose (relative/change)
Fasting plasma/serum insulin (absolute values)
+1 more
Secondary study objectives
Continuous glucose monitoring (CGM) profile
Fasting serum or plasma free fatty acids (FFA) (absolute values)
Fasting serum or plasma free fatty acids (FFA) (relative/change)
+4 more
Other study objectives
Deuterium tracer enrichment in body water (measured in blood)
Deuterium tracer enrichment in body water (measured in saliva)
Hepatic de novo lipogenesis (absolute values)
+1 more

Trial Design

3Treatment groups
Experimental Treatment
Placebo Group
Group I: Diazoxide oral suspension, 2 mg per kg per doseExperimental Treatment3 Interventions
Participants will ingest diazoxide oral suspension at 2 mg per kg body weight per dose (27 doses over 14 days). Blinding will occur by completely covering single-dose oral syringes with labels.
Group II: Diazoxide oral suspension, 1 mg per kg per doseExperimental Treatment3 Interventions
Participants will ingest diazoxide oral suspension at 1 mg per kg body weight per dose (27 doses over 14 days). Blinding will occur by completely covering single-dose oral syringes with labels.
Group III: PlaceboPlacebo Group3 Interventions
Participants will ingest a placebo solution (27 doses over 14 days) formulated to approximate the taste of diazoxide oral suspension. Blinding will occur by completely covering single-dose oral syringes with labels.
Treatment
First Studied
Drug Approval Stage
How many patients have taken this drug
FreeStyle Libre Pro
2023
Completed Phase 1
~30

Find a Location

Who is running the clinical trial?

Columbia UniversityLead Sponsor
1,498 Previous Clinical Trials
2,767,071 Total Patients Enrolled
University of California, BerkeleyOTHER
187 Previous Clinical Trials
640,922 Total Patients Enrolled
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)NIH
2,463 Previous Clinical Trials
4,337,349 Total Patients Enrolled
Joshua R Cook, MD, PhDPrincipal InvestigatorColumbia University
8 Previous Clinical Trials
176 Total Patients Enrolled

Media Library

Diazoxide (Potassium Channel Activator) Clinical Trial Eligibility Overview. Trial Name: NCT05729282 — Phase 1
Incretin Hormones in Polycystic Ovary Syndrome Research Study Groups: Placebo, Diazoxide oral suspension, 1 mg per kg per dose, Diazoxide oral suspension, 2 mg per kg per dose
Incretin Hormones in Polycystic Ovary Syndrome Clinical Trial 2023: Diazoxide Highlights & Side Effects. Trial Name: NCT05729282 — Phase 1
Diazoxide (Potassium Channel Activator) 2023 Treatment Timeline for Medical Study. Trial Name: NCT05729282 — Phase 1
~16 spots leftby Aug 2025