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Treatment for Sanfilippo Syndrome

N/A

Recruiting

Research Sponsored by Lysosomal and Rare Disorders Research and Treatment Center, Inc.

Eligibility Criteria Checklist

Specific guidelines that determine who can or cannot participate in a clinical trial

Must have

Timeline

Screening 3 weeks

Treatment Varies

Follow Up 6 months

Awards & highlights

No Placebo-Only Group

The natural history study of patients with Sanfilippo disease(s) (MPS3)

Eligible Conditions

Screening ~ 3 weeks3 visits

Treatment ~ Varies

Follow Up ~ 6 months

Screening ~ 3 weeks

Treatment ~ Varies

Follow Up ~6 months

This trial's timeline: 3 weeks for screening, Varies for treatment, and 6 months for reporting.

Study objectives can provide a clearer picture of what you can expect from a treatment.

Primary study objectives

To characterize the disease natural history in patients with MPS3.

No Placebo-Only Group

All patients enrolled in this study will receive some form of active treatment.

Do I qualify?Apply below to find out

Lysosomal and Rare Disorders Research and Treatment Center, Inc.Lead Sponsor

8 Previous Clinical Trials

100,330 Total Patients Enrolled

Team SanfilippoUNKNOWN

1 Previous Clinical Trials

10 Total Patients Enrolled

1 Trials studying Sanfilippo Syndrome

10 Patients Enrolled for Sanfilippo Syndrome

~0 spots leftby Dec 2024

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