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Phase 3 Trials
Substrate Reduction Therapy
Venglustat for Fabry Disease
Recruiting2 awardsPhase 3
Atlanta, Georgia
This trial is an 18-month study to evaluate the effect of a new therapy on a heart issue in adults with Fabry Disease. Participants visit every 3-6 months and may continue in the study for up to 18 more months.
Substrate Reduction Therapy
Long-term Safety of Lucerastat for Fabry Disease
Recruiting2 awardsPhase 3
Birmingham, Alabama
This trial is testing the safety and tolerability of a medication called lucerastat, which is taken by mouth. It is aimed at adults with Fabry disease, a condition where harmful fats build up in the body. Lucerastat helps to reduce these fat levels.
Trials With No Placebo
Substrate Reduction Therapy
Venglustat for Fabry Disease
Recruiting2 awardsPhase 3
Atlanta, Georgia
This trial is an 18-month study to evaluate the effect of a new therapy on a heart issue in adults with Fabry Disease. Participants visit every 3-6 months and may continue in the study for up to 18 more months.
Gene Therapy
Gene Therapy for Fabry Disease
Recruiting1 awardPhase 1 & 2
Atlanta, Georgia
This trial tests ST-920, a treatment using a virus to deliver a gene that helps produce an important enzyme in patients with Fabry disease. The goal is to help these patients by continuously making the enzyme to reduce harmful substances in their bodies. ST-920 is a gene therapy treatment for Fabry disease, which aims to deliver a gene to produce the enzyme alpha-galactosidase A, addressing the enzyme deficiency central to the disease.
Frequently Asked Questions
Do I need insurance to participate in a trial?
Almost all clinical trials will cover the cost of the 'trial drug' — so no insurance is required for this. For trials where this trial drug is given alongside an already-approved medication, there may be a cost (which your insurance would normally cover).
Is there any support for travel costs?
Many of the teams running clinical trials will cover the cost of transportation to-and-from their care center.
Will I know what medication I am taking?
This depends on the specific study. If you're worried about receiving a placebo, you can actively filter out these trials using our search.
How long do clinical trials last?
Some trials will only require a single visit, while others will continue until your disease returns. It's fairly common for a trial to last somewhere between 1 and 6 months.
Do you verify all the trials on your website?
All of the trials listed on Power have been formally registered with the US Food and Drug Administration. Beyond this, some trials on Power have been formally 'verified' if the team behind the trial has completed an additional level of verification with our team.
How quickly will I hear back from a clinical trial?
Sadly, this response time can take anywhere from 6 hours to 2 weeks. We're working hard to speed up how quickly you hear back — in general, verified trials respond to patients within a few days.