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PI3K Inhibitor

Health-related Quality of Life, Symptom Severity, and Pain Among Patients With PIK3CA-related Overgrowth Spectrum: A Mixed-methods Observational Study

East Hanover, NJ
N/A
Waitlist Available
Research Sponsored by Novartis Pharmaceuticals
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
Timeline
Screening 3 weeks
Treatment Varies
Follow Up 4 months
Awards & highlights
No Placebo-Only Group

Summary

This is a mixed-methods observational study that incorporates both qualitative interviews and quantitative data collection through a web-based longitudinal survey (day 1, months 2 and 4).

See full description

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~4 months
This trial's timeline: 3 weeks for screening, Varies for treatment, and 4 months for reporting.

Treatment Details

Study Objectives

Study objectives can provide a clearer picture of what you can expect from a treatment.
Primary study objectives
Brief Pain Inventory for Adult Self-Report and Adolescent Self-Report
EQ-5D-5L for Adult self-report
EQ-5D-Youth for adolescent Self-Report and Caregiver-Proxy
+5 more
Secondary study objectives
Description of change in HRQoL, symptom severity, and pain as a result of treatment

Awards & Highlights

No Placebo-Only Group
All patients enrolled in this study will receive some form of active treatment.

Trial Design

2Treatment groups
Experimental Treatment
Group I: PROS patients treated with alpelisibExperimental Treatment1 Intervention
Patients with PROS who receive treatment with alpelisb
Group II: PROS patients not treated with alpelisibExperimental Treatment0 Interventions
Patients with PROS who don't receive treatment with apelisib

Find a Location

Closest Location:Novartis Investigative Site· East Hanover, NJ· 459 miles

Who is running the clinical trial?

Novartis PharmaceuticalsLead Sponsor
2,960 Previous Clinical Trials
4,274,614 Total Patients Enrolled
~16 spots leftby Mar 2026