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Thrombopoietin Receptor Agonist

Avatrombopag for Thrombocytopenia in Gastrointestinal Cancer (ACT-GI Trial)

Phase 2
Recruiting
Led By Gerald A Soff, MD
Research Sponsored by Hanny Al-Samkari, MD
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
Be older than 18 years old
Timeline
Screening 3 weeks
Treatment Varies
Follow Up at baseline, days 8 +/-1 and 15 +/-1

Summary

This trial will compare how well these drugs work to treat CIT in patients with GI malignancies receiving chemotherapy.

Who is the study for?
This trial is for adults with gastrointestinal cancers who are undergoing chemotherapy and have a low platelet count, known as Chemotherapy-Induced Thrombocytopenia (CIT). They must not have certain blood disorders or be planning to receive other investigational drugs. Participants should not be pregnant, breastfeeding, or have had recent bleeding events.
What is being tested?
The study compares Avatrombopag, a drug that stimulates platelet production, against a placebo in patients with CIT from GI cancer treatments. The goal is to see if Avatrombopag can better manage low platelet counts during chemotherapy cycles.
What are the potential side effects?
Potential side effects of Avatrombopag may include headache, fatigue, bruising or bleeding more easily than normal. As it affects blood clotting processes, there could also be risks of developing blood clots.

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~at baseline, days 8 +/-1 and 15 +/-1
This trial's timeline: 3 weeks for screening, Varies for treatment, and at baseline, days 8 +/-1 and 15 +/-1 for reporting.

Treatment Details

Study Objectives

Study objectives can provide a clearer picture of what you can expect from a treatment.
Primary study objectives
Response Rate
Response Rate of CIT Treatment in Avatrombopag
Response Rate of CIT Treatment in Placebo Group
Secondary study objectives
Proportion of Platelet Count Recovery in Avatrombopag Group
Proportion of Platelet Count Recovery in Placebo Group
Rate of Clinically Relevant Bleeding Events in Avatrombopag Group
+7 more

Side effects data

From 2014 Phase 3 trial • 49 Patients • NCT01438840
38%
Headache
31%
Contusion
19%
Upper respiratory tract infection
13%
Gingival bleeding
13%
Arthralgia
13%
Fatigue
13%
Epistaxis
13%
Petechiae
9%
Nasopharyngitis
9%
Mouth Haemorrhage
9%
Insomnia
9%
Nausea
9%
Back pain
6%
Influenza
6%
Anaemia
6%
Thrombocytopenia
6%
Vomiting
6%
Blood gastrin increased
6%
Cough
6%
Hypertension
3%
Dyspepsia
3%
Cerebrovascular accident
3%
Mouth haemorrhage
3%
Food poisoning
3%
Polyserositis
3%
Uterine haemorrhage
3%
Urinary tract infection
3%
Platelet count decreased
3%
Deep vein thrombosis
3%
Pain in extremity
100%
80%
60%
40%
20%
0%
Study treatment Arm
Avatrombopag (Core Study)
Avatrombopag (Extension Phase)
Placebo (Core Study)

Trial Design

2Treatment groups
Experimental Treatment
Active Control
Group I: Group A - AvatromopagExperimental Treatment1 Intervention
30 participants will be randomized into a 1:1 fashion and will be stratified based on the number of cytotoxic agents in the patient's chemotherapy regimen. Participants will complete study procedures as outlined: Lead-In Period (Day 1 - 15) * Pre-determined dose of Avatrombopag 1x daily. * Participants failing to achieve a platelet count ≥100,000/µL within 2 weeks will be considered a treatment failure (and will proceed to the end-of-study visit). On-Cycle Period (Day 15 - up to Week 6) • Pre-determined dose of Avatrombopag 1x daily. Follow-up Period * End of Treatment on-site visit. * Follow-up visit 30-42 days after End of Treatment visit.
Group II: Group B - Matching PlaceboActive Control1 Intervention
30 participants will be randomized into a 1:1 fashion and will be stratified based on the number of cytotoxic agents in the patient's chemotherapy regimen. Participants will complete study procedures as outlined: Lead-In Period (Day 1 - 15) * Pre-determined dose of matching placebo 1x daily. * Participants failing to achieve a platelet count ≥100,000/µL within 2 weeks will be considered a treatment failure (and will proceed to the end-of-study visit). On-Cycle Period (Day 15 - up to Week 6) • Pre-determined dose of matching placebo 1x daily. Follow-up Period * End of Treatment on-site visit. * Follow-up visit 30-42 days after End of Treatment visit.
Treatment
First Studied
Drug Approval Stage
How many patients have taken this drug
Avatrombopag
2016
Completed Phase 3
~490

Find a Location

Who is running the clinical trial?

Hanny Al-Samkari, MDLead Sponsor
1 Previous Clinical Trials
33 Total Patients Enrolled
Swedish Orphan BiovitrumIndustry Sponsor
100 Previous Clinical Trials
13,088 Total Patients Enrolled
Gerald A Soff, MDPrincipal InvestigatorUniversity of Miami Cancer Center

Media Library

Avatrombopag (Thrombopoietin Receptor Agonist) Clinical Trial Eligibility Overview. Trial Name: NCT05772546 — Phase 2
Gastrointestinal Cancer Research Study Groups: Group A - Avatromopag, Group B - Matching Placebo
Gastrointestinal Cancer Clinical Trial 2023: Avatrombopag Highlights & Side Effects. Trial Name: NCT05772546 — Phase 2
Avatrombopag (Thrombopoietin Receptor Agonist) 2023 Treatment Timeline for Medical Study. Trial Name: NCT05772546 — Phase 2
~11 spots leftby Mar 2025