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Unknown

ARD-101 for Prader-Willi Syndrome

Phase 2
Waitlist Available
Research Sponsored by Aardvark Therapeutics, Inc.
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
No history of ketoacidosis or hyperosmolar coma
PWS due to chromosome 15 micro-deletion, maternal uniparental disomy, or imprinting defect, confirmed by fluorescent in situ hybridization, chromosomal microarray, and/or methylation studies
Must not have
Diagnosis of type 1 diabetes mellitus or other active endocrine disorders (e.g., Cushing syndrome, or thyroid dysfunction except if on stable adequate thyroid or glucocorticoid replacement supplement)
Liver disease or liver injury as indicated by abnormal liver function tests, SGOT (aspartate aminotransferase (AST)), alkaline phosphatase, or serum bilirubin (> 1.5 x upper limit of normal (ULN) for any of these tests) or history of hepatic cirrhosis
Timeline
Screening 3 weeks
Treatment Varies
Follow Up baseline, day 15, day 28
Awards & highlights
No Placebo-Only Group

Summary

This trial is testing a new drug to treat Prader-Willi Syndrome, a rare genetic disorder that causes intellectual disability, behavior problems, and obesity. The trial will assess the safety and efficacy of the drug in patients with the syndrome.

Who is the study for?
This trial is for individuals aged 17-65 with Prader-Willi Syndrome, a stable body weight, and no history of severe mental health issues or substance abuse. Participants must not be on insulin but can use certain other diabetes medications if doses have been stable. They should not have significant organ disease or recent medical treatments that could affect the study.
What is being tested?
The trial is testing ARD-101, an oral medication for Prader-Willi Syndrome. It's a Phase 2 study where all participants receive the drug to see how safe it is and how well it works (since there's no comparison group).
What are the potential side effects?
While specific side effects are not listed here, common concerns in trials like this may include digestive discomfort, potential blood sugar changes, and possible allergic reactions.

Eligibility Criteria

Inclusion Criteria

You may be eligible if you check “Yes” for the criteria below
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I have never had ketoacidosis or hyperosmolar coma.
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My PWS is confirmed by specific genetic tests.
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I am between 17 and 65 years old.

Exclusion Criteria

You may be eligible for the trial if you check “No” for criteria below:
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I have type 1 diabetes or another hormone-related condition but am on stable medication.
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My liver is not functioning properly, as shown by my test results.
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My kidney function is impaired, as shown by abnormal test results or a calculation.
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I have a history of serious bleeding problems.
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I do not have any serious liver, kidney, lung, heart, cancer, or stomach/intestine diseases.

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~baseline, day 15, day 28
This trial's timeline: 3 weeks for screening, Varies for treatment, and baseline, day 15, day 28 for reporting.

Treatment Details

Study Objectives

Study objectives can provide a clearer picture of what you can expect from a treatment.
Primary study objectives
Incidence of Treatment-Emergent Adverse Events (TEAE)
Secondary study objectives
Effect on Weight
Efficacy Evaluation of Hyperphagia in Prader-Willi Syndrome
Other study objectives
Change in Body Fat
Change in GI Passage
Change in Patient Health
+5 more

Side effects data

From 2023 Phase 2 trial • 12 Patients • NCT05215847
17%
Mild Nausea
8%
Mild Constipation
8%
Mild Headache
8%
Mild Heart Burn
8%
Mild Hypoglycemia
8%
Mild Dyspepsia
8%
Mild Common Cold
8%
Mild COVID-19
8%
Mild Emesis
100%
80%
60%
40%
20%
0%
Study treatment Arm
ARD-101

Awards & Highlights

No Placebo-Only Group
All patients enrolled in this study will receive some form of active treatment.

Trial Design

1Treatment groups
Experimental Treatment
Group I: ARD-101Experimental Treatment1 Intervention
First week 400 mg of ARD-101 twice daily, second week 600 mg of ARD-101 twice daily, third week 800 mg of ARD-101 twice daily, fourth week 800 mg of ARD-101 twice daily.
Treatment
First Studied
Drug Approval Stage
How many patients have taken this drug
ARD-101
2021
Completed Phase 2
~40

Find a Location

Who is running the clinical trial?

Aardvark Therapeutics, Inc.Lead Sponsor
3 Previous Clinical Trials
44 Total Patients Enrolled
Children's Hospital ColoradoOTHER
120 Previous Clinical Trials
5,133,173 Total Patients Enrolled
Stanford UniversityOTHER
2,491 Previous Clinical Trials
17,518,146 Total Patients Enrolled
1 Trials studying Prader-Willi Syndrome

Media Library

ARD-101 (Unknown) Clinical Trial Eligibility Overview. Trial Name: NCT05153434 — Phase 2
Prader-Willi Syndrome Research Study Groups: ARD-101
Prader-Willi Syndrome Clinical Trial 2023: ARD-101 Highlights & Side Effects. Trial Name: NCT05153434 — Phase 2
ARD-101 (Unknown) 2023 Treatment Timeline for Medical Study. Trial Name: NCT05153434 — Phase 2
~5 spots leftby Jan 2026