← Back to Search

Small Molecule

PTC518 for Huntington's Disease

Phase 2
Waitlist Available
Research Sponsored by PTC Therapeutics
Eligibility Criteria Checklist
Specific guidelines that determine who can or cannot participate in a clinical trial
Must have
Be older than 18 years old
Timeline
Screening 3 weeks
Treatment Varies
Follow Up up to 5 years
Awards & highlights
No Placebo-Only Group

Summary

This trial aims to study the long-term safety and effects of PTC518 in individuals with Huntington's disease.

Who is the study for?
This trial is specifically for individuals who have Huntington's Disease and have already completed the treatment period in a prior study, PTC518-CNS-002-HD. It's not open to those who haven't participated in that initial study.
What is being tested?
The focus of this extension study is on assessing the long-term safety and effectiveness of a drug called PTC518 for people with Huntington's Disease who were previously involved in an earlier phase of research.
What are the potential side effects?
Since this summary doesn't provide specific side effects, it can be assumed that participants will be monitored for any long-term adverse reactions to PTC518 as part of evaluating its safety.

Timeline

Screening ~ 3 weeks
Treatment ~ Varies
Follow Up ~up to 5 years
This trial's timeline: 3 weeks for screening, Varies for treatment, and up to 5 years for reporting.

Treatment Details

Awards & Highlights

No Placebo-Only Group
All patients enrolled in this study will receive some form of active treatment.

Trial Design

3Treatment groups
Experimental Treatment
Group I: PTC518 5 mgExperimental Treatment1 Intervention
Participants will receive PTC518 5 mg tablets once daily orally for 24 months.
Group II: PTC518 20 mgExperimental Treatment1 Intervention
Participants will receive PTC518 20 mg tablets once daily orally for 24 months.
Group III: PTC518 10 mgExperimental Treatment1 Intervention
Participants will receive PTC518 10 mg tablets once daily orally for 24 months.

Find a Location

Who is running the clinical trial?

PTC TherapeuticsLead Sponsor
74 Previous Clinical Trials
6,037 Total Patients Enrolled
~167 spots leftby Jun 2027
Unbiased ResultsWe believe in providing patients with all the options.
Your Data Stays Your DataWe only share your information with the clinical trials you're trying to access.
Verified Trials OnlyAll of our trials are run by licensed doctors, researchers, and healthcare companies.
Back to top